Correction of the pathogenic mutation in TGM1 gene by adenine base editing in mutant embryos-Reference-Cited by-同舟云学术

Correction of the pathogenic mutation in TGM1 gene by adenine base editing in mutant embryos

Published:2022-01 Issue:1 Volume:30 Page:175-183
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Dang Lu,Zhou Xueliang,Zhong Xiufang,Yu Wenxia,Huang Shisheng,Liu Hanyan,Chen Yuanyuan,Zhang Wuwen,Yuan Lihua,Li Lei,Huang Xingxu,Li Guanglei,Liu Jianqiao,Tong Guoqing

Funder

Leading Talents Program of Guangdong Province

National Natural Science Foundation of China

National Key Research and Development Program of China

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference43 articles.

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5. Preclinical Evaluation of a Modified Herpes Simplex Virus Type 1 Vector Encoding Human TGM1 for the Treatment of Autosomal Recessive Congenital Ichthyosis;Freedman;J. Invest. Dermatol.,2021

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