Targeted Repair of CYBB in X-CGD iPSCs Requires Retention of Intronic Sequences for Expression and Functional Correction-Reference-Cited by-同舟云学术

Targeted Repair of CYBB in X-CGD iPSCs Requires Retention of Intronic Sequences for Expression and Functional Correction

Published:2017-02 Issue:2 Volume:25 Page:321-330
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Sweeney Colin L.,Zou Jizhong,Choi Uimook,Merling Randall K.,Liu Alexander,Bodansky Aaron,Burkett Sandra,Kim Jung-Woong,De Ravin Suk See,Malech Harry L.

Funder

National Institute of Allergy and Infectious Diseases

National Institutes of Health

National Cancer Institute

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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5. Oxidase-deficient neutrophils from X-linked chronic granulomatous disease iPS cells: functional correction by zinc finger nuclease-mediated safe harbor targeting;Zou;Blood,2011

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