CRISPR/Cas9 Editing of the Mutant Huntingtin Allele In Vitro and In Vivo-Reference-Cited by-同舟云学术

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CRISPR/Cas9 Editing of the Mutant Huntingtin Allele In Vitro and In Vivo

Published:2017-01 Issue:1 Volume:25 Page:12-23
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Monteys Alex Mas,Ebanks Shauna A.,Keiser Megan S.,Davidson Beverly L.

Funder

Hoppy’s Hope Foundation

Philly Cure HD

The Leslie Gehry Brenner Prize

The Foerderer Grant for Excellence

NIH

The Children’s Hospital of Philadelphia Research Institute

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference44 articles.

1. Huntington’s disease;Walker;Semin. Neurol.,2007

2. Mild experimental brain injury in the rat induces cognitive deficits associated with regional neuronal loss in the hippocampus;Hicks;J. Neurotrauma,1993

3. Huntington’s disease: progress toward effective disease-modifying treatments and a cure;Johnson;Hum. Mol. Genet.,2010

4. Reversal of neuropathology and motor dysfunction in a conditional model of Huntington’s disease;Yamamoto;Cell,2000

5. Full motor recovery despite striatal neuron loss and formation of irreversible amyloid-like inclusions in a conditional mouse model of Huntington’s disease;Díaz-Hernández;J. Neurosci.,2005

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