Cas9 editing of ATXN1 in a spinocerebellar ataxia type 1 mice and human iPSC-derived neurons
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Published:2024-12
Issue:4
Volume:35
Page:102317
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ISSN:2162-2531
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Container-title:Molecular Therapy - Nucleic Acids
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language:en
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Short-container-title:Molecular Therapy - Nucleic Acids
Author:
Fagan Kelly J.,
Chillon Guillem,
Carrell Ellie M.,
Waxman Elisa A.,
Davidson Beverly L.ORCID