B-Cell Depletion and Immunomodulation before Initiation of Enzyme Replacement Therapy Blocks the Immune Response to Acid Alpha-Glucosidase in Infantile-Onset Pompe Disease-Reference-Cited by-同舟云学术

B-Cell Depletion and Immunomodulation before Initiation of Enzyme Replacement Therapy Blocks the Immune Response to Acid Alpha-Glucosidase in Infantile-Onset Pompe Disease

Published:2013-09 Issue:3 Volume:163 Page:847-854.e1
ISSN:0022-3476
Container-title:The Journal of Pediatrics
language:en
Short-container-title:The Journal of Pediatrics

Author:

Elder Melissa E.,Nayak Sushrusha,Collins Shelley W.,Lawson Lee Ann,Kelley Jeffry S.,Herzog Roland W.,Modica Renee F.,Lew Judy,Lawrence Robert M.,Byrne Barry J.

Publisher

Elsevier BV

Subject

Pediatrics, Perinatology and Child Health

Reference23 articles.

1. Pompe disease: design, methodology, and early findings from the Pompe Registry;Byrne;Mol Genet Metab,2011

2. Predicting cross-reactive immunological material (CRIM) status in Pompe disease using GAA mutations: lessons learned from 10 years of clinical laboratory testing experience;Bali;Am J Med Genet C Semin Med Genet,2012

3. High antibody titer in an adult with Pompe disease affects treatment with alglucosidase alfa;de Vries;Mol Genet Metab,2010

4. Cross-reactive immunologic material status affects treatment outcomes in Pompe disease infants;Kishnani;Mol Genet Metab,2010

5. Successful immune tolerance induction to enzyme replacement therapy in CRIM-negativeinfantile Pompe disease;Messinger;Genet Med,2012

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