Discussing investigational AAV gene therapy with hemophilia patients: A guide
Author:
Funder
Spark Therapeutics, Philadelphia, PA, USA
Publisher
Elsevier BV
Subject
Oncology,Hematology
Reference107 articles.
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2. Establishing the prevalence and prevalence at birth of hemophilia in males: a meta-analytic approach using national registries;Iorio;Ann Intern Med,2019
3. Kreuth III: European consensus proposals for treatment of haemophilia with coagulation factor concentrates;Giangrande;Haemophilia.,2014
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