Hemophilia gene therapy: first, do no harm-Reference-Cited by-同舟云学术

Hemophilia gene therapy: first, do no harm

Published:2023-09 Issue:9 Volume:21 Page:2354-2361
ISSN:1538-7836
Container-title:Journal of Thrombosis and Haemostasis
language:en
Short-container-title:Journal of Thrombosis and Haemostasis

Author:

Valentino Leonard A.^ORCID,Kaczmarek Radoslaw^ORCID,Pierce Glenn F.^ORCID,Noone Declan^ORCID,O’Mahony Brian^ORCID,Page David^ORCID,Rotellini Dawn^ORCID,Skinner Mark W.^ORCID

Funder

Bayer

Spark Therapeutics

Publisher

Elsevier BV

Subject

Hematology

Reference99 articles.

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3. ISTH subcommittee on Factor VIII, Factor IX, rare bleeding disorders. Core data set on safety, efficacy, and durability of hemophilia gene therapy for a global registry: communication from the SSC of the ISTH;Konkle;J Thromb Haemost,2020

4. Cost-effectiveness analysis of recombinant factor IX Fc fusion protein compared with recombinant factor IX for the treatment of moderate-severe to severe hemophilia B in China;Zhou;Pediatr Blood Cancer,2023

5. The cost of hemophilia treatment: the importance of minimizing it without detriment to its quality;Rodriguez-Merchan;Expert Rev Hematol,2020

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