Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial-Reference-Cited by-同舟云学术

Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial

Published:2022-10 Issue:10 Volume:9 Page:e724-e732
ISSN:2352-3026
Container-title:The Lancet Haematology
language:en
Short-container-title:The Lancet Haematology

Author:

Glenthøj Andreas,van Beers Eduard J,Al-Samkari Hanny,Viprakasit Vip,Kuo Kevin H M,Galactéros Frédéric,Chonat Satheesh,Porter John,Zagadailov Erin,Xu Rengyi,Oluyadi Abdulafeez,Hawkins Peter,Gheuens Sarah,Beynon Vanessa,Barcellini Wilma

Funder

Agios Pharmaceuticals

Publisher

Elsevier BV

Subject

Hematology

Reference25 articles.

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3. Comorbidities and complications in adults with pyruvate kinase deficiency;Boscoe;Eur J Haematol,2021

4. Clinical spectrum of pyruvate kinase deficiency: data from the Pyruvate Kinase Deficiency Natural History Study;Grace;Blood,2018

5. Prevalence and management of iron overload in pyruvate kinase deficiency: report from the Pyruvate Kinase Deficiency Natural History Study;van Beers;Haematologica,2019

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