Efficacy and Safety of Mitapivat in Pyruvate Kinase Deficiency: A Systematic Review and Meta-analysis of Clinical Trials
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Publisher
Springer Science and Business Media LLC
Link
https://link.springer.com/content/pdf/10.1007/s12288-024-01830-x.pdf
Reference29 articles.
1. Pyruvate (2023) Kinase Deficiency - Symptoms, Causes, Treatment | NORD. Accessed December 4, https://rarediseases.org/rare-diseases/pyruvate-kinase-deficiency/
2. Zahra K, Dey T, Ashish, Mishra SP, Pandey U (2020) Pyruvate kinase M2 and cancer: the role of PKM2 in promoting tumorigenesis. Front Oncol 10:159. https://doi.org/10.3389/fonc.2020.00159
3. Grace RF, Rose C, Layton DM et al (2019) Safety and efficacy of mitapivat in pyruvate kinase deficiency. N Engl J Med 381(10):933–944. https://doi.org/10.1056/NEJMoa1902678
4. Glenthøj A, van Beers EJ, Al-Samkari H et al (2022) Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial. Lancet Haematol 9(10):e724–e732. https://doi.org/10.1016/S2352-3026(22)00214-9
5. Secrest MH, Storm M, Carrington C et al (2020) Prevalence of pyruvate kinase deficiency: a systematic literature review. Eur J Haematol 105(2):173–184. https://doi.org/10.1111/ejh.13424
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