Improved molecular platform for the gene therapy of rare diseases by liver protein secretion-Reference-Cited by-同舟云学术

Improved molecular platform for the gene therapy of rare diseases by liver protein secretion

Published:2018-11 Issue:11 Volume:61 Page:723-728
ISSN:1769-7212
Container-title:European Journal of Medical Genetics
language:en
Short-container-title:European Journal of Medical Genetics

Author:

Quiviger Mickael,Giannakopoulos Aristeidis,Verhenne Sebastien,Marie Corinne,Stavrou Eleana F.,Vanhoorelbeke Karen,Izsvák Zsuzsanna,De Meyer Simon F.,Athanassiadou Aglaia,Scherman Daniel^ORCID

Funder

E-RARE ERANET

TRANSPOSMART CONSORTIUM

Publisher

Elsevier BV

Subject

Genetics (clinical),Genetics,General Medicine

Reference50 articles.

1. Development of S/MAR minicircles for enhanced and persistent transgene expression in the mouse liver;Argyros;J. Mol. Med.,2011

2. Long-term therapeutic levels of human α-1 antitrypsin in plasma after hydrodynamic injection of nonviral DNA;Aliño;Gene Ther. Sep,2003

3. Secreted human placental alkaline phosphatase as a reporter gene for in vivo gene transfer;Bettan;Anal. Biochem.,1999

4. Plasmid DNA electrotransfer for intracellular and secreted proteins expression: new methodological developments and applications;Bloquel;J Gene Med. Feb,2004

5. Minicircle DNA vectors devoid of bacterial DNA result in persistent and high-level transgene expression in vivo;Chen;Mol. Ther,2003

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