Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Iduronate-2-Sulfatase in Rhesus Macaques-Reference-Cited by-同舟云学术

登录注册会员服务联系我们

Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Iduronate-2-Sulfatase in Rhesus Macaques

Published:2018-09 Issue: Volume:10 Page:68-78
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Hordeaux Juliette,Hinderer Christian,Goode Tamara,Buza Elizabeth L.,Bell Peter,Calcedo Roberto,Richman Laura K.,Wilson James M.

Funder

University of Pennsylvania

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference27 articles.

1. Clinical efficacy of enzyme replacement therapy in paediatric Hunter patients, an independent study of 3.5 years;Tomanin;Orphanet J. Rare Dis.,2014

2. The mucopolysaccharidoses;Neufeld,2001

3. Cognitive and behaviour profiles of children with mucopolysaccharidosis Type II;Crowe;Cogn. Neuropsychol.,2017

4. Enzymatic replacement therapy for Hunter disease: Up to 9 years experience with 17 patients;Parini;Mol. Genet. Metab. Rep.,2015

5. A phase I/II study of intrathecal idursulfase-IT in children with severe mucopolysaccharidosis II;Muenzer;Genet. Med.,2016

Cited by 64 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Restoration of peripheral neuropathy in Fabry mice via intrathecal administration of an adeno-associated virus vector encoding mGLA cDNA;Molecular Genetics and Metabolism;2024-09

2. A minimally invasive endovascular approach to the cerebellopontine angle cistern enables broad CNS biodistribution of scAAV9-CB-GFP;Molecular Therapy;2024-08

3. The potential of gene delivery for the treatment of traumatic brain injury;Journal of Neuroinflammation;2024-07-28

4. Prenatal AAV9-GFP administration in fetal lambs results in transduction of female germ cells and maternal exposure to virus;Molecular Therapy - Methods & Clinical Development;2024-06

5. Adeno-associated virus as a delivery vector for gene therapy of human diseases;Signal Transduction and Targeted Therapy;2024-04-03

同舟云学术

1.学者识别学者识别

2.学术分析学术分析

3.人才评估人才评估

"同舟云学术"是以全球学者为主线，采集、加工和组织学术论文而形成的新型学术文献查询和分析系统，可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容，当前同舟云学术共收录了国内外主流学术期刊6万余种，收集的期刊论文及会议论文总量共计约1.5亿篇，并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询！咨询电话：010-8811{复制后删除}0370

www.globalauthorid.com

TOP

Copyright © 2019-2024 北京同舟云网络信息技术有限公司
京公网安备11010802033243号京ICP备18003416号-3