A phase I/II study of intrathecal idursulfase-IT in children with severe mucopolysaccharidosis II-Reference-Cited by-同舟云学术

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A phase I/II study of intrathecal idursulfase-IT in children with severe mucopolysaccharidosis II

Published:2016-01 Issue:1 Volume:18 Page:73-81
ISSN:1098-3600
Container-title:Genetics in Medicine
language:en
Short-container-title:Genetics in Medicine

Author:

Muenzer Joseph,Hendriksz Christian J.,Fan Zheng,Vijayaraghavan Suresh,Perry Victor,Santra Saikat,Solanki Guirish A.,Mascelli Mary Ann,Pan Luying,Wang Nan,Sciarappa Kenneth,Barbier Ann J.

Publisher

Elsevier BV

Subject

Genetics (clinical)

Link

http://www.nature.com/articles/gim201536.pdf

Reference20 articles.

1. The mucopolysaccharidoses.;Neufeld,2001

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