Mutant allele knockout with novel CRISPR nuclease promotes myelopoiesis in ELANE neutropenia-Reference-Cited by-同舟云学术

Mutant allele knockout with novel CRISPR nuclease promotes myelopoiesis in ELANE neutropenia

Published:2022-09 Issue: Volume:26 Page:119-131
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Sabo Peter,Makaryan Vahagn,Dicken Yosef,Povodovski Lital,Rockah Liat,Bar Tzlil,Gabay Matan,Elinger Dalia,Segal Ella,Haimov Ora,Antoshvili Maya,Drori Anat London,Poulsen Tanoya,Herman Asael,Emmanuel Rafi,Dale David C.^ORCID

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference52 articles.

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5. Mutations in the ELA2 gene correlate with more severe expression of neutropenia: a study of 81 patients from the French Neutropenia Register;Bellanné-Chantelot;Blood,2004

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