CRISPR-Cas9n-mediated ELANE promoter editing for gene therapy of severe congenital neutropenia
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Published:2024-06
Issue:6
Volume:32
Page:1628-1642
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ISSN:1525-0016
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Container-title:Molecular Therapy
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language:en
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Short-container-title:Molecular Therapy
Author:
Nasri Masoud,
Ritter Malte U.,
Mir Perihan,
Dannenmann Benjamin,
Kaufmann Masako M.,
Arreba-Tutusaus Patricia,
Xu Yun,
Borbaran-Bravo Natalia,
Klimiankou Maksim,
Lengerke Claudia,
Zeidler Cornelia,
Cathomen Toni,
Welte Karl,
Skokowa JuliaORCID
Cited by
2 articles.
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