Integrating HDAd5/35++ Vectors as a New Platform for HSC Gene Therapy of Hemoglobinopathies-Reference-Cited by-同舟云学术

Integrating HDAd5/35++ Vectors as a New Platform for HSC Gene Therapy of Hemoglobinopathies

Published:2018-06 Issue: Volume:9 Page:142-152
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Li Chang,Psatha Nikoletta,Wang Hongjie,Singh Manvendra,Samal Himanshu Bhusan,Zhang Wenli,Ehrhardt Anja,Izsvák Zsuzsanna,Papayannopoulou Thalia,Lieber André

Funder

Wings of Karen” Foundation

Marsha Rivkin Foundation

Cooley’s Anemia Foundation

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference51 articles.

1. Global epidemiology of haemoglobin disorders and derived service indicators;Modell;Bull. W. H. O.,2008

2. Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia;Cavazzana-Calvo;Nature,2010

3. Correction of beta-thalassemia major by gene transfer in haematopoietic progenitors of pediatric patients;Roselli;EMBO Mol. Med.,2010

4. Potentially therapeutic levels of anti-sickling globin gene expression following lentivirus-mediated gene transfer in sickle cell disease bone marrow CD34+ cells;Urbinati;Exp. Hematol.,2015

5. Gene therapy approaches for hemoglobinopathies;Ferrari;Hematol. Oncol. Clin,2017

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