Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectors-Reference-Cited by-同舟云学术

Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectors

Published:2022-12 Issue: Volume:27 Page:272-280
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Horiuchi Makoto,Hinderer Christian J.,Greig Jenny A.,Dyer Cecilia,Buza Elizabeth L.,Bell Peter,Chichester Jessica A.,Hayashi Peter M.,Yan Hanying,Goode Tamara,Wilson James M.^ORCID

Funder

Janssen Pharmaceuticals

Janssen Pharmaceutical Companies of Johnson and Johnson

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference31 articles.

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2. Hepatotoxicity following administration of onasemnogene abeparvovec (AVXS-101) for the treatment of spinal muscular atrophy;Chand;J. Hepatol.,2021

3. Widespread gene transfer in the central nervous system of cynomolgus macaques following delivery of AAV9 into the cisterna magna;Hinderer;Mol. Ther. Methods Clin. Dev.,2014

4. Translational feasibility of lumbar puncture for intrathecal AAV administration;Hinderer;Mol. Ther. Methods Clin. Dev.,2020

5. Kinetics and MR-based monitoring of AAV9 vector delivery into cerebrospinal fluid of nonhuman primates;Ohno;Mol. Ther. Methods Clin. Dev.,2019

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