Hepatotoxicity following administration of onasemnogene abeparvovec (AVXS-101) for the treatment of spinal muscular atrophy-Reference-Cited by-同舟云学术

Hepatotoxicity following administration of onasemnogene abeparvovec (AVXS-101) for the treatment of spinal muscular atrophy

Published:2021-03 Issue:3 Volume:74 Page:560-566
ISSN:0168-8278
Container-title:Journal of Hepatology
language:en
Short-container-title:Journal of Hepatology

Author:

Chand Deepa,Mohr Franziska,McMillan Hugh^ORCID,Tukov Francis Fonyuy^ORCID,Montgomery Kyle,Kleyn Aaron,Sun Rui,Tauscher-Wisniewski Sitra,Kaufmann Petra,Kullak-Ublick Gerd

Funder

Novartis Gene Therapies

Publisher

Elsevier BV

Subject

Hepatology

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4. Spinal muscular atrophy: a timely review;Kolb;Arch Neurol,2011

5. Spinal muscular atrophy: journeying from bench to bedside;Awano;Neurotherapeutics,2014

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