Biosafety Studies of a Clinically Applicable Lentiviral Vector for the Gene Therapy of Artemis-SCID-Reference-Cited by-同舟云学术

Biosafety Studies of a Clinically Applicable Lentiviral Vector for the Gene Therapy of Artemis-SCID

Published:2019-12 Issue: Volume:15 Page:232-245
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Charrier Sabine,Lagresle-Peyrou Chantal,Poletti Valentina,Rothe Michael^ORCID,Cédrone Grégory,Gjata Bernard,Mavilio Fulvio^ORCID,Fischer Alain,Schambach Axel,de Villartay Jean-Pierre,Cavazzana Marina,Hacein-Bey-Abina Salima,Galy Anne

Funder

INSERM/DGOS

European Union’s FP7 research and innovation programme

French Muscular Dystrophy Association/Telethon

“Region Ile-de-France,”

“Conseil General de l'Essonne,”

Genopole

Evry University

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference29 articles.

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2. Artemis, a novel DNA double-strand break repair/V(D)J recombination protein, is mutated in human severe combined immune deficiency;Moshous;Cell,2001

3. The etalol-beta-lactamase/beta-CASP domain of Artemis constitutes the catalytic core for V(D)J recombination;Poinsignon;J. Exp. Med.,2004

4. Interplay between Ku, Artemis, and the DNA-dependent protein kinase catalytic subunit at DNA ends;Drouet;J. Biol. Chem.,2006

5. DNA replication stress triggers rapid DNA replication fork breakage by Artemis and XPF;Bétous;PloS Genet.,2018

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