Effective Multi-lineage Engraftment in a Mouse Model of Fanconi Anemia Using Non-genotoxic Antibody-Based Conditioning-Reference-Cited by-同舟云学术

Effective Multi-lineage Engraftment in a Mouse Model of Fanconi Anemia Using Non-genotoxic Antibody-Based Conditioning

Published:2020-06 Issue: Volume:17 Page:455-464
ISSN:2329-0501
Container-title:Molecular Therapy - Methods & Clinical Development
language:en
Short-container-title:Molecular Therapy - Methods & Clinical Development

Author:

Srikanthan Meera A.,Humbert Olivier,Haworth Kevin G.,Ironside Christina,Rajawat Yogendra S.,Blazar Bruce R.,Palchaudhuri Rahul,Boitano Anthony E.,Cooke Michael P.,Scadden David T.,Kiem Hans-Peter

Funder

Markey Molecular Medicine Investigator

Jose Carreras/E. Donnall Thomas Endowed Chair for Cancer Research

Endowed Chair for Stem Cell and Gene Therapy

’s endowment fund

Magenta Therapeutics

National Heart, Lung, and Blood Institute

National Institutes of Health

NIH/NCI Cancer Center

Publisher

Elsevier BV

Subject

Genetics,Molecular Biology,Molecular Medicine

Reference28 articles.

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2. Recent discoveries in the molecular pathogenesis of the inherited bone marrow failure syndrome Fanconi anemia;Mamrak;Blood Rev.,2017

3. Pathophysiology and management of inherited bone marrow failure syndromes;Shimamura;Blood Rev.,2010

4. Alternative donor hematopoietic cell transplantation for Fanconi anemia;MacMillan;Blood,2015

5. Hematopoietic cell transplantation in Fanconi anemia: current evidence, challenges and recommendations;Ebens;Expert Rev. Hematol.,2017

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