Author:
Shah Apeksha M,Al-Chalabi Ammar
Reference5 articles.
1. Patisiran, an RNAi therapeutic, for hereditary transthyretin amyloidosis;Adams;N Engl J Med,2018
2. Inotersen treatment for patients with hereditary transthyretin amyloidosis;Benson;N Engl J Med,2018
3. In vivo genome editing improves motor function and extends survival in a mouse model of ALS;Gaj;Sci Adv,2017
4. Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy;Amoasii;Science,2018
5. Subcutaneous immunoglobulin for maintenance treatment in chronic inflammatory demyelinating polyneuropathy (PATH): a randomised, double-blind, placebo-controlled, phase 3 trial;van Schaik;Lancet Neurol,2018
Cited by
1 articles.
订阅此论文施引文献
订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献