Systemic mRNA Therapy for the Treatment of Fabry Disease: Preclinical Studies in Wild-Type Mice, Fabry Mouse Model, and Wild-Type Non-human Primates-Reference-Cited by-同舟云学术

Systemic mRNA Therapy for the Treatment of Fabry Disease: Preclinical Studies in Wild-Type Mice, Fabry Mouse Model, and Wild-Type Non-human Primates

Published:2019-04 Issue:4 Volume:104 Page:625-637
ISSN:0002-9297
Container-title:The American Journal of Human Genetics
language:en
Short-container-title:The American Journal of Human Genetics

Author:

Zhu Xuling,Yin Ling,Theisen Matt,Zhuo Jenny,Siddiqui Summar,Levy Becca,Presnyak Vladimir,Frassetto Andrea,Milton Jaclyn,Salerno Timothy,Benenato Kerry E.,Milano Joe,Lynn Andy,Sabnis Staci,Burke Kristine,Besin Gilles,Lukacs Christine M.,Guey Lin T.,Finn Patrick F.,Martini Paolo G.V.

Publisher

Elsevier BV

Subject

Genetics(clinical),Genetics

Reference51 articles.

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