Rescue of a familial dysautonomia mouse model by AAV9-Exon-specific U1 snRNA-Reference-Cited by-同舟云学术

Rescue of a familial dysautonomia mouse model by AAV9-Exon-specific U1 snRNA

Published:2022-08 Issue:8 Volume:109 Page:1534-1548
ISSN:0002-9297
Container-title:The American Journal of Human Genetics
language:en
Short-container-title:The American Journal of Human Genetics

Author:

Romano Giulia,Riccardi Federico,Bussani Erica,Vodret Simone,Licastro Danilo,Ragone Isabella,Ronzitti Giuseppe,Morini Elisabetta,Slaugenhaupt Susan A.,Pagani Franco^ORCID

Publisher

Elsevier BV

Subject

Genetics (clinical),Genetics

Reference92 articles.

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