Modeling the Early Phenotype at the Neuromuscular Junction of Spinal Muscular Atrophy Using Patient-Derived iPSCs-Reference-Cited by-同舟云学术

Modeling the Early Phenotype at the Neuromuscular Junction of Spinal Muscular Atrophy Using Patient-Derived iPSCs

Published:2015-04 Issue:4 Volume:4 Page:561-568
ISSN:2213-6711
Container-title:Stem Cell Reports
language:en
Short-container-title:Stem Cell Reports

Author:

Yoshida Michiko,Kitaoka Shiho,Egawa Naohiro,Yamane Mayu,Ikeda Ryunosuke,Tsukita Kayoko,Amano Naoki,Watanabe Akira,Morimoto Masafumi,Takahashi Jun,Hosoi Hajime,Nakahata Tatsutoshi,Inoue Haruhisa,Saito Megumu K.

Funder

Ministry of Health, Labour and Welfare of Japan

Ministry of Education, Culture, Sports, Science and Technology of Japan

Ministry of Education, Culture, Sports, Science and Technology

Japan Society for the Promotion of Science

Japan Science and Technology Agency (JST)

CREST

JST

Japan Research Foundation for Clinical Pharmacology

Mochida Memorial Foundation for Medical and Pharmaceutical Research

Intramural Research Grant

Publisher

Elsevier BV

Subject

Cell Biology,Developmental Biology,Genetics,Biochemistry

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3. Brief report: phenotypic rescue of induced pluripotent stem cell-derived motoneurons of a spinal muscular atrophy patient;Chang;Stem Cells,2011

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5. Genetic correction of human induced pluripotent stem cells from patients with spinal muscular atrophy;Corti;Sci. Transl. Med.,2012

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