Author:
Chen Agnes H.,Harmatz Paul,Nestrasil Igor,Eisengart Julie B.,King Kelly E.,Rudser Kyle,Kaizer Alexander M.,Svatkova Alena,Wakumoto Amy,Le Steven Q.,Madden Jacqueline,Young Sarah,Zhang Haoyue,Polgreen Lynda E.,Dickson Patricia I.
Funder
Ryan Foundation
Sanofi Genzyme/Biomarin JV
NIH
National Center for Advancing Translational Science
UCSF CTSI
University of Pennsylvania
Lysosomal Disease Network
Rare Diseases Clinical Research Network
Office of Rare Diseases Research
NCATS
NINDS
NIDDK
Subject
Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism
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