1. Blood and Marrow Transplantation Program, Department of Pediatrics, University Medical Center Utrecht, Utrecht, The Netherlands;
2. Blood and Marrow Transplant Unit, Royal Manchester Children's Hospital, Manchester, United Kingdom;
3. Program in Blood and Marrow Transplantation, University of Minnesota, Minneapolis, MN;
4. Department of Hematology and Bone Marrow Transplantation, Our Lady's Children's Hospital, Dublin, Ireland;
5. Blood and Marrow Transplantation Program, Great Ormond Street Hospital for Children National Health Service Trust, London, United Kingdom;
6. Département de Biothérapie and
7. Reference Center for Inherited Metabolic Diseases and Imagine Institute, Assistance Publique-Hopiteaux de Paris, Hôpital Universitaire Necker-Enfants Malades, Paris, France;
8. Pediatric Bone Marrow Transplant Unit, Department of Pediatrics, San Gerardo University Hospital, Monza, Italy;
9. The Pediatric Blood and Marrow Transplant Program, Duke University, Durham, NC;
10. Willink Unit, Manchester Centre for Genomic Medicine, Central Manchester University Hospitals, University of Manchester, Manchester, United Kingdom;
11. Rare Metabolic Disorders Unit, Department of Pediatrics, San Gerardo University Hospital, Monza, Italy;
12. Pediatric Hematology and Oncology, University Hospital Leuven, Leuven, Belgium;
13. Pediatric Hematology and Oncology, Ghent University Hospital, Ghent, Belgium;
14. Department of Pediatric Immunology and Rheumatology, University Medical Center Utrecht, Utrecht, The Netherlands;
15. University Groningen, University Medical Center Groningen, Department of Genetics, Groningen, The Netherlands; and
16. Department of Pediatrics and Neurology, Division of Clinical Behavioral Neuroscience, University of Minnesota, Minneapolis, MN