Consensus statement on preventive and symptomatic care of leukodystrophy patients-Reference-Cited by-同舟云学术

Consensus statement on preventive and symptomatic care of leukodystrophy patients

Published:2015-04 Issue:4 Volume:114 Page:516-526
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Van Haren Keith^ORCID,Bonkowsky Joshua L.,Bernard Genevieve,Murphy Jennifer L.,Pizzino Amy,Helman Guy^ORCID,Suhr Dean,Waggoner Jacque,Hobson Don,Vanderver Adeline,Patterson Marc C.

Funder

Members of the Leukodystrophy Alliance

The Department of Genetics, Children's National Health System, Washington DC, and Marshall Summar

The Department of Neurology, Children's National Health System, Washington DC, and Phillip Pearl

National Organization for Rare Disorders

Montreal Children's Hospital and McGill University Health Center Research Institutes

RMAG (Réseau de Médecine Génétique Appliquée)

Fondation sur les Leucodystrophies

Fondation du Grand Défi Pierre Lavoie

Fondation Les Amis D'Élliot

Fondation Désirée le Papillon, Genome Canada

Canadian Institutes of Health Research

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

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2. Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy;Cartier;Science,2009

3. Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy;Biffi;Science,2013

4. Neural stem cell engraftment and myelination in the human brain;Gupta;Sci. Transl. Med.,2012

5. Managing cystic fibrosis: strategies that increase life expectancy and improve quality of life;Cohen-Cymberknoh;Am. J. Respir. Crit. Care Med.,2011

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