Long-term nonsense suppression therapy moderates MPS I-H disease progression-Reference-Cited by-同舟云学术

Long-term nonsense suppression therapy moderates MPS I-H disease progression

Published:2014-03 Issue:3 Volume:111 Page:374-381
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Gunn Gwen,Dai Yanying,Du Ming,Belakhov Valery,Kandasamy Jeyakumar,Schoeb Trenton R.,Baasov Timor,Bedwell David M.,Keeling Kim M.

Funder

University of Pennsylvania “Improved Therapies for MPS I Grant Program”

NIH

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference42 articles.

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