Enzyme replacement therapy (ERT) procedure for mucopolysaccharidosis type II (MPS II) by intraventricular administration (IVA) in murine MPS II-Reference-Cited by-同舟云学术

Enzyme replacement therapy (ERT) procedure for mucopolysaccharidosis type II (MPS II) by intraventricular administration (IVA) in murine MPS II

Published:2012-09 Issue:1-2 Volume:107 Page:122-128
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Higuchi Takashi,Shimizu Hiromi,Fukuda Takahiro,Kawagoe Shiho,Matsumoto Juri,Shimada Yohta,Kobayashi Hiroshi,Ida Hiroyuki,Ohashi Toya,Morimoto Hideto,Hirato Tohru,Nishino Katsuya,Eto Yoshikatsu

Funder

Japanese Ministry of Health, Labor, and Welfare

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference33 articles.

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2. Japan Elaprase Treatment (JET) study: idursulfase enzyme replacement therapy in adult patients with attenuated Hunter syndrome (Mucopolysaccharidosis II, MPS II);Okuyama;Mol. Genet. Metab.,2010

3. Long-term enzyme replacement therapy in a severe case of mucopolysaccharidosis type II (Hunter syndrome);Papadia;Eur. Rev. Med. Pharmacol. Sci.,2011

4. Gaucher disease: outcome following total hip replacements and effect of enzyme replacement therapy in a cohort of UK patients;Donaldson;Hip Int.,2011

5. Enzyme replacement therapy for Pompe disease;Angelini;Curr. Neurol. Neurosci. Rep.,2012

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