Author:
Vera Moin U.,Le Steven Q.,Victoroff Alla,Passage Merry B.,Brown Jillian R.,Crawford Brett E.,Polgreen Lynda E.,Chen Agnes H.,Dickson Patricia I.
Funder
Zacharon Pharmaceuticals
National Institute of Neurological Disorders and Stroke
Lysosomal Disease Network
The Lysosomal Disease Network
National Institute of Health (NIH) Rare Diseases Clinical Research Network
NIH Office of Rare Diseases Research
National Center for Advancing Translational Science
National Institute of Diabetes and Digestive and Kidney Diseases
Subject
Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism
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