Early initiation of enzyme replacement therapy for the mucopolysaccharidoses
Author:
Publisher
Elsevier BV
Subject
Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism
Reference88 articles.
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3. Expression of the disease on female carriers of X-linked lysosomal disorders: a brief review;Pinto;Orphanet J. Rare Dis.,2010
4. Long-term efficacy and safety of laronidase in the treatment of mucopolysaccharidosis I;Clarke;Pediatrics,2009
5. Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5years: results of a multinational study of recombinant human alpha-l-iduronidase (laronidase);Wraith;Pediatrics,2007
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