Spinal cord compression in young children with type VI mucopolysaccharidosis

Author:

Horovitz Dafne Dain Gandelman,Magalhães Tatiana de Sá Pacheco Carneiro,e Costa Alessandra Pena,Carelli Luis Eduardo,e Silva Daniel Souza,de Linhares e Riello Anna Patricia Freitas,Llerena Juan Clinton

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference33 articles.

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3. A new dysostosis with urinary excretion of chondroitin-sulphate B;Maroteaux;Presse Med.,1963

4. Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double blinded, placebo-controlled, multinational study of recombinant human alpha-l-iduronidase (laronidase);Wraith;J. Pediatr.,2004

5. The first 5years of clinical experience with laronidase enzyme replacement therapy for mucopolysaccharidosis I;Wraith;Expert. Opin. Pharmacother.,2005

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1. Mucopolisacaridosis tipo VI: a propósito de un caso;Revista de la Asociación Argentina de Ortopedia y Traumatología;2023-04-24

2. Burden of Surgical Treatment for the Management of Cervical Myelopathy in Mucopolysaccharidoses: A Systematic Review;Brain Sciences;2022-12-26

3. Spinal cord compression in patients with mucopolysaccharidosis;European Spine Journal;2022-03-10

4. Non-cardiac Manifestations in Adult Patients With Mucopolysaccharidosis;Frontiers in Cardiovascular Medicine;2022-03-07

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