CNS-targeted AAV5 gene transfer results in global dispersal of vector and prevention of morphological and function deterioration in CNS of globoid cell leukodystrophy mouse model-Reference-Cited by-同舟云学术

CNS-targeted AAV5 gene transfer results in global dispersal of vector and prevention of morphological and function deterioration in CNS of globoid cell leukodystrophy mouse model

Published:2011-08 Issue:4 Volume:103 Page:367-377
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

Lin Dar-Shong,Hsiao Chung-Der,Liau Ian,Lin Shuan-Pei,Chiang Ming-Fu,Chuang Chih-Kuang,Wang Tuen-Jen,Wu Tsu-Yen,Jian Yuan-Ren,Huang Sung-Fa,Liu Hsuan-Liang

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

Reference47 articles.

1. Globoid cell leucodystrophy (Krabbe's disease): deficiency of galactocerebroside beta-galactosidase;Suzuki;Proc. Natl. Acad. Sci. U.S.A.,1970

2. Molecular genetics of Krabbe disease (globoid cell leukodystrophy): diagnostic and clinical implications;Wenger;Hum. Mutat.,1997

3. Murine model of genetic demyelinating disease: the twitcher mouse;Suzuki;Microsc. Res. Technol.,1995

4. The twitcher mouse. Central nervous system pathology after bone marrow transplantation;Suzuki;Lab. Invest.,1988

5. The long-term outcomes of presymptomatic infants transplanted for Krabbe disease: report of the workshop held on July 11 and 12, 2008, Holiday Valley, New York;Duffner;Genet. Med.,2009

Cited by 23 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Brain Targeted AAV1-GALC Gene Therapy Reduces Psychosine and Extends Lifespan in a Mouse Model of Krabbe Disease;Genes;2023-07-25

2. Rapamycin Alleviates Protein Aggregates, Reduces Neuroinflammation, and Rescues Demyelination in Globoid Cell Leukodystrophy;Cells;2023-03-24

3. Various AAV Serotypes and Their Applications in Gene Therapy: An Overview;Cells;2023-03-01

4. Preclinical studies in Krabbe disease: A model for the investigation of novel combination therapies for lysosomal storage diseases;Molecular Therapy;2023-01

5. Krabbe Disease: Prospects of Finding a Cure Using AAV Gene Therapy;Frontiers in Medicine;2021-11-11