Cognitive endpoints for therapy development for neuronopathic mucopolysaccharidoses: Results of a consensus procedure-Reference-Cited by-同舟云学术

Cognitive endpoints for therapy development for neuronopathic mucopolysaccharidoses: Results of a consensus procedure

Published:2017-06 Issue:2 Volume:121 Page:70-79
ISSN:1096-7192
Container-title:Molecular Genetics and Metabolism
language:en
Short-container-title:Molecular Genetics and Metabolism

Author:

van der Lee Johanna H.,Morton Jonathan,Adams Heather R.,Clarke Lorne,Ebbink Berendine Johanne,Escolar Maria L.,Giugliani Roberto,Harmatz Paul,Hogan Melissa^ORCID,Jones Simon,Kearney Shauna,Muenzer Joseph,Rust Stewart,Semrud-Clikeman Margaret,Wijburg Frits A.,Yu Zi-fan,Janzen Darren,Shapiro Elsa^ORCID

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology,Biochemistry,Endocrinology, Diabetes and Metabolism

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