Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome-Reference-Cited by-同舟云学术

Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome

Published:2018-05 Issue:9 Volume:23 Page:2606-2616
ISSN:2211-1247
Container-title:Cell Reports
language:en
Short-container-title:Cell Reports

Author:

Kuo Caroline Y.^ORCID,Long Joseph D.,Campo-Fernandez Beatriz,de Oliveira Satiro,Cooper Aaron R.,Romero Zulema,Hoban Megan D.,Joglekar Alok V.,Lill Georgia R.,Kaufman Michael L.,Fitz-Gibbon Sorel,Wang Xiaoyan,Hollis Roger P.,Kohn Donald B.

Funder

California Institute for Regenerative Medicine

Clinical Immunology Society

UCLA Children’s Discovery and Innovation Institute Today’s and Tomorrow’s Children Fund

Primary Immune Deficiency Treatment Consortium

NIH

UCLA K12 Child Health Research Center

Hyper-IgM Foundation

Eli & Edythe Broad Center of Regenerative Medicine and Stem Cell Research

Interdisciplinary Training in Virology and Gene Therapy

Whitcome Predoctoral Training Program

UCLA Molecular Biology Institute

Ruth L. Kirschstein National Research Service

Publisher

Elsevier BV

Subject

General Biochemistry, Genetics and Molecular Biology

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