International Society for Cell & Gene Therapy Stem Cell Engineering Committee report on the current state of hematopoietic stem and progenitor cell–based genomic therapies and the challenges faced-Reference-Cited by-同舟云学术

International Society for Cell & Gene Therapy Stem Cell Engineering Committee report on the current state of hematopoietic stem and progenitor cell–based genomic therapies and the challenges faced

Published:2024-06 Issue: Volume: Page:
ISSN:1465-3249
Container-title:Cytotherapy
language:en
Short-container-title:Cytotherapy

Author:

Gupta Ashish O.^ORCID,Azul Melissa^ORCID,Bhoopalan Senthil Velan^ORCID,Abraham Allistair^ORCID,Bertaina Alice,Bidgoli Alan^ORCID,Bonfim Carmem,DeZern Amy,Li Jingjing^ORCID,Louis Chrystal U.,Purtill Duncan,Ruggeri Annalisa,Boelens Jaap Jan,Prockop Susan,Sharma Akshay^ORCID

Funder

American Society of Hematology

National Cancer Institute

National Heart Lung and Blood Institute

National Institutes of Health

St. Jude Children's Research Hospital

American Lebanese Syrian Associated Charities

National Institute of Diabetes and Digestive and Kidney Diseases

Publisher

Elsevier BV

Reference154 articles.

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3. Long-term outcomes after allogeneic hematopoietic stem cell transplantation for metachromatic leukodystrophy: the largest single-institution cohort report;Boucher;Orphanet J Rare Dis,2015

4. Survival and functional outcomes in boys with cerebral adrenoleukodystrophy with and without hematopoietic stem cell transplantation;Raymond;Biol Blood Marrow Transplant,2019

5. Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium;Thakar;Lancet,2023