Design of novel small molecule base-pair recognizers of toxic CUG RNA transcripts characteristics of DM1-Reference-Cited by-同舟云学术

Design of novel small molecule base-pair recognizers of toxic CUG RNA transcripts characteristics of DM1

Published:2021 Issue: Volume:19 Page:51-61
ISSN:2001-0370
Container-title:Computational and Structural Biotechnology Journal
language:en
Short-container-title:Computational and Structural Biotechnology Journal

Author:

Ondono Raul,Lirio Ángel,Elvira Carlos,Álvarez-Marimon Elena,Provenzano Claudia,Cardinali Beatrice,Pérez-Alonso Manuel,Perálvarez-Marín Alex,Borrell José I.,Falcone Germana,Estrada-Tejedor Roger

Funder

“la Caixa” Foundation

Instituto de Salud Carlos III

Publisher

Elsevier BV

Subject

Computer Science Applications,Genetics,Biochemistry,Structural Biology,Biophysics,Biotechnology

Reference52 articles.

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4. Association Between Mutation Size and Cardiac Involvement in Myotonic Dystrophy Type 1: An Analysis of the DM1-Heart Registry;Chong-Nguyen;Circ Cardiovasc Genet,2017

5. André LM, Van Cruchten RTP, Willemse M, Wansink DG. (CTG)n repeat-mediated dysregulation of MBNL1 and MBNL2 expression during myogenesis in DM1 occurs already at the myoblast stage. PLoS One 2019;14:1–17. https://doi.org/10.1371/journal.pone.0217317.

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