Time-controlled and muscle-specific CRISPR/Cas9-mediated deletion of CTG-repeat expansion in the DMPK gene-Reference-Cited by-同舟云学术

Time-controlled and muscle-specific CRISPR/Cas9-mediated deletion of CTG-repeat expansion in the DMPK gene

Published:2022-03 Issue: Volume:27 Page:184-199
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Cardinali Beatrice^ORCID,Provenzano Claudia^ORCID,Izzo Mariapaola^ORCID,Voellenkle Christine^ORCID,Battistini Jonathan^ORCID,Strimpakos Georgios^ORCID,Golini Elisabetta^ORCID,Mandillo Silvia^ORCID,Scavizzi Ferdinando^ORCID,Raspa Marcello^ORCID,Perfetti Alessandra^ORCID,Baci Denisa^ORCID,Lazarevic Dejan^ORCID,Garcia-Manteiga Jose Manuel^ORCID,Gourdon Geneviève,Martelli Fabio^ORCID,Falcone Germana^ORCID

Funder

Telethon Italy

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

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