Delivery of Cas9-guided ABE8e into stem cells using poly(l-lysine) polypeptides for correction of the hemophilia-associated FIX missense mutation
Author:
Publisher
Elsevier BV
Subject
Cell Biology,Molecular Biology,Biochemistry,Biophysics
Reference28 articles.
1. The hemophilias--from royal genes to gene therapy;Mannucci;N. Engl. J. Med.,2001
2. Guidelines working group on behalf of the world federation of, guidelines for the management of hemophilia;Srivastava;Haemophilia,2013
3. Hemophilia B gene therapy with a high-specific-activity factor IX variant;George;N. Engl. J. Med.,2017
4. Immune responses to AAV vectors: overcoming barriers to successful gene therapy;Mingozzi;Blood,2013
5. Potential of induced pluripotent stem cells for use in gene therapy: history, molecular bases, and medical perspectives;Fus-Kujawa;Biomolecules,2021
Cited by 5 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. DNA base editing corrects common hemophilia A mutations and restores factor VIII expression in in vitro and ex vivo models;Journal of Thrombosis and Haemostasis;2024-08
2. Gene editing in liver diseases;FEBS Letters;2024-07-30
3. The research progress of correcting pathogenic mutations by base editing;Obstetrics and Gynecology;2024-05-06
4. Applying the CRISPR/Cas9 for Treating Human and Animal Diseases – Comprehensive Review;Annals of Animal Science;2023-11-01
5. Treatment of congenital coagulopathies, from biologic to biotechnological drugs: The relevance of gene editing (CRISPR/Cas);Thrombosis Research;2023-11
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3