Efficient Gene Editing at Major CFTR Mutation Loci-Reference-Cited by-同舟云学术

Efficient Gene Editing at Major CFTR Mutation Loci

Published:2019-06 Issue: Volume:16 Page:73-81
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Ruan Jinxue,Hirai Hiroyuki,Yang Dongshan,Ma Linyuan,Hou Xia,Jiang Hong,Wei Hongguang,Rajagopalan Carthic,Mou Hongmei,Wang Guoshun,Zhang Jifeng,Li Kui,Chen Yuqing E.,Sun Fei,Xu Jie

Funder

Cystic Fibrosis Foundation Therapeutics award

NIH

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

Reference27 articles.

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2. Origins of cystic fibrosis lung disease;Stoltz;N. Engl. J. Med.,2015

3. Identification of the cystic fibrosis gene: chromosome walking and jumping;Rommens;Science,1989

4. A CFTR potentiator in patients with cystic fibrosis and the G551D mutation;Ramsey;N. Engl. J. Med.,2011

5. Lumacaftor-Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del CFTR;Wainwright;N. Engl. J. Med.,2015

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