Preclinical characterization of antagomiR-218 as a potential treatment for myotonic dystrophy
Author:
Funder
Carlos III Health Institute
Publisher
Elsevier BV
Subject
Drug Discovery,Molecular Medicine
Reference74 articles.
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4. Identification and characterization of modified antisense oligonucleotides targeting DMPK in mice and nonhuman primates for the treatment of myotonic dystrophy type 1;Pandey;J. Pharmacol. Exp. Ther.,2015
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