Identification and Characterization of Modified Antisense Oligonucleotides Targeting DMPK in Mice and Nonhuman Primates for the Treatment of Myotonic Dystrophy Type 1-Reference-Cited by-同舟云学术

Identification and Characterization of Modified Antisense Oligonucleotides Targeting DMPK in Mice and Nonhuman Primates for the Treatment of Myotonic Dystrophy Type 1

Published:2015-09-01 Issue:2 Volume:355 Page:329-340
ISSN:0022-3565
Container-title:Journal of Pharmacology and Experimental Therapeutics
language:en
Short-container-title:J Pharmacol Exp Ther

Author:

Pandey Sanjay K.,Wheeler Thurman M.,Justice Samantha L.,Kim Aneeza,Younis Husam S.,Gattis Danielle,Jauvin Dominic,Puymirat Jack,Swayze Eric E.,Freier Susan M.,Bennett C. Frank,Thornton Charles A.,MacLeod A. Robert

Publisher

American Society for Pharmacology & Experimental Therapeutics (ASPET)

Subject

Pharmacology,Molecular Medicine

Reference54 articles.

1. Toxicologic Effects of an Oligodeoxynucleotide Phosphorothioate and Its Analogs Following Intravenous Administration in Rats

2. RNA Targeting Therapeutics: Molecular Mechanisms of Antisense Oligonucleotides as a Therapeutic Platform

3. DMPK dosage alterations result in atrioventricular conduction abnormalities in a mouse myotonic dystrophy model

4. Function and Genetics of Dystrophin and Dystrophin-Related Proteins in Muscle

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