Imprecision Medicine: A One-Size-Fits-Many Approach for Muscle Dystrophy
Author:
Publisher
Elsevier BV
Subject
Cell Biology,Genetics,Molecular Medicine
Reference9 articles.
1. Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63% of patients with Duchenne muscular dystrophy
2. Therapy for Duchenne muscular dystrophy: renewed optimism from genetic approaches
3. Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy
4. In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy
5. Dystrophin levels as low as 30% are sufficient to avoid muscular dystrophy in the human
Cited by 4 articles. 订阅此论文施引文献 订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献
1. Current Genetic Survey and Potential Gene-Targeting Therapeutics for Neuromuscular Diseases;International Journal of Molecular Sciences;2020-12-16
2. Determination of qPCR Reference Genes Suitable for Normalizing Gene Expression in a Canine Model of Duchenne Muscular Dystrophy;Journal of Neuromuscular Diseases;2018-05-29
3. Effective regeneration of dystrophic muscle using autologous iPSC-derived progenitors with CRISPR-Cas9 mediated precise correction;Medical Hypotheses;2018-01
4. Recent developments in Duchenne muscular dystrophy: facts and numbers;J CACHEXIA SARCOPENI;2017
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