High-level correction of the sickle mutation is amplified in vivo during erythroid differentiation
Author:
Funder
National Institutes of Health
California Institute for Regenerative Medicine
Li Ka Shing Foundation
Heritage Medical Research Institute
Publisher
Elsevier BV
Subject
Multidisciplinary
Reference52 articles.
1. A machine learning approach for predicting CRISPR-Cas9 cleavage efficiencies and patterns underlying its mechanism of action;Abadi;PLoS Comput. Biol.,2017
2. Long-term survival of ex-thalassemic patients with persistent mixed chimerism after bone marrow transplantation;Andreani;Bone Marrow Transpl.,2000
3. Quantitatively different red cell/nucleated cell chimerism in patients with long-term, persistent hematopoietic mixed chimerism after bone marrow transplantation for thalassemia major or sickle cell disease;Andreani;Haematologica,2011
4. ATF4 regulates MYB to increase γ-globin in response to loss of β-globin;Boontanrart;Cell Rep.,2020
5. Near-optimal probabilistic RNA-seq quantification;Bray;Nat. Biotech.,2016
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