Adenovirus-mediated gene transfer and expression of human -glucuronidase gene in the liver, spleen, and central nervous system in mucopolysaccharidosis type VII mice-Reference-Cited by-同舟云学术

Adenovirus-mediated gene transfer and expression of human -glucuronidase gene in the liver, spleen, and central nervous system in mucopolysaccharidosis type VII mice

Published:1997-02-18 Issue:4 Volume:94 Page:1287-1292
ISSN:0027-8424
Container-title:Proceedings of the National Academy of Sciences
language:en
Short-container-title:Proceedings of the National Academy of Sciences

Author:

Ohashi T.,Watabe K.,Uehara K.,Sly W. S.,Vogler C.,Eto Y.

Publisher

Proceedings of the National Academy of Sciences

Subject

Multidisciplinary

Reference45 articles.

1. REVERSAL OF CLINICAL FEATURES OF HURLER'S DISEASE AND BIOCHEMICAL IMPROVEMENT AFTER TREATMENT BY BONE-MARROW TRANSPLANTATION

2. Marrow Transplantation in Genetic Disease

3. Treatment of genetic defects in hematopoietic cell function by gene transfer

4. Beta glucuronidase deficiency: Report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis

5. Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency.

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