Identification of an Allosteric Binding Site on Human Lysosomal Alpha-Galactosidase Opens the Way to New Pharmacological Chaperones for Fabry Disease-Reference-Cited by-同舟云学术

Identification of an Allosteric Binding Site on Human Lysosomal Alpha-Galactosidase Opens the Way to New Pharmacological Chaperones for Fabry Disease

Published:2016-10-27 Issue:10 Volume:11 Page:e0165463
ISSN:1932-6203
Container-title:PLOS ONE
language:en
Short-container-title:PLoS ONE

Author:

Citro Valentina,Peña-García Jorge,den-Haan Helena,Pérez-Sánchez Horacio,Del Prete Rosita,Liguori Ludovica,Cimmaruta Chiara,Lukas Jan,Cubellis Maria Vittoria^ORCID,Andreotti Giuseppina

Funder

Fondazione Telethon

Fundación Séneca

NLHPC

Publisher

Public Library of Science (PLoS)

Subject

Multidisciplinary

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5. Functional and Clinical Consequences of Novel alpha-Galactosidase A Mutations in Fabry Disease;J Lukas;Hum Mutat,2016

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