Peptide-conjugated phosphodiamidate oligomer-mediated exon skipping has benefits for cardiac function in mdx and Cmah-/-mdx mouse models of Duchenne muscular dystrophy-Reference-Cited by-同舟云学术

Peptide-conjugated phosphodiamidate oligomer-mediated exon skipping has benefits for cardiac function in mdx and Cmah-/-mdx mouse models of Duchenne muscular dystrophy

Published:2018-06-18 Issue:6 Volume:13 Page:e0198897
ISSN:1932-6203
Container-title:PLOS ONE
language:en
Short-container-title:PLoS ONE

Author:

Blain Alison M.^ORCID,Greally Elizabeth,McClorey Graham,Manzano Raquel,Betts Corinne A.^ORCID,Godfrey Caroline,O’Donovan Liz,Coursindel Thibault,Gait Mike J.,Wood Matthew J.,MacGowan Guy A.,Straub Volker W.

Funder

AFM-Téléthon

Publisher

Public Library of Science (PLoS)

Subject

Multidisciplinary

Reference29 articles.

1. Population frequencies of inherited neuromuscular diseases—a world survey;A Emery;Neuromsucular Disorders,1991

2. The molecular defect in Duchenne muscular dystrophy;JKJ Tomkins;Muscle Nerve,1980

3. Isolation of candidate cDNAs for portions of the Duchenne muscular dystrophy gene;APA Monaco;Nature,1986

4. Dystrophin and mutations: one gene, several proteins, multiple phenotypes;FF Muntoni;Lancet Neurol,2003

5. Clinical variability in Becker muscular dystrophy Genetic, biochemical and immunohistochemical correlates;GP Comi;Brain,1994

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