Systemic PPMO-mediated dystrophin expression in the Dup2 mouse model of Duchenne muscular dystrophy-Reference-Cited by-同舟云学术

Systemic PPMO-mediated dystrophin expression in the Dup2 mouse model of Duchenne muscular dystrophy

Published:2022-12 Issue: Volume:30 Page:479-492
ISSN:2162-2531
Container-title:Molecular Therapy - Nucleic Acids
language:en
Short-container-title:Molecular Therapy - Nucleic Acids

Author:

Gushchina Liubov V.,Vetter Tatyana A.,Frair Emma C.,Bradley Adrienne J.^ORCID,Grounds Kelly M.^ORCID,Lay Jacob W.,Huang Nianyuan,Suhaiba Aisha^ORCID,Schnell Frederick J.,Hanson Gunnar,Simmons Tabatha R.,Wein Nicolas^ORCID,Flanigan Kevin M.

Publisher

Elsevier BV

Subject

Drug Discovery,Molecular Medicine

Reference45 articles.

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4. Entries in the Leiden Duchenne muscular dystrophy mutation database: an overview of mutation types and paradoxical cases that confirm the reading-frame rule;Aartsma-Rus;Muscle Nerve,2006

5. Duplications in the DMD gene;White;Hum. Mutat.,2006

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