The Pharmacological Chaperone AT2220 Increases Recombinant Human Acid α-Glucosidase Uptake and Glycogen Reduction in a Mouse Model of Pompe Disease-Reference-Cited by-同舟云学术

The Pharmacological Chaperone AT2220 Increases Recombinant Human Acid α-Glucosidase Uptake and Glycogen Reduction in a Mouse Model of Pompe Disease

Published:2012-07-18 Issue:7 Volume:7 Page:e40776
ISSN:1932-6203
Container-title:PLoS ONE
language:en
Short-container-title:PLoS ONE

Author:

Khanna Richie,Flanagan John J.,Feng Jessie,Soska Rebecca,Frascella Michelle,Pellegrino Lee J.,Lun Yi,Guillen Darlene,Lockhart David J.,Valenzano Kenneth J.

Publisher

Public Library of Science (PLoS)

Subject

Multidisciplinary

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4. Pompe disease in infants and children.;PS Kishnani;J Pediatr,2004

5. Chinese hamster ovary cell-derived recombinant human acid alpha-glucosidase in infantile-onset pompe disease.;PS Kishnani;J Pediatr,2006

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