Genetically engineered probiotic for the treatment of phenylketonuria (PKU); assessment of a novel treatment in vitro and in the PAHenu2 mouse model of PKU
Author:
Funder
National PKU Alliance
National Society for PKU
Publisher
Public Library of Science (PLoS)
Subject
Multidisciplinary
Reference28 articles.
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2. Low therapeutic threshold for hepatocyte replacement in murine phenylketonuria;K Hamman;Mol Ther,2005
3. Bone impairment in phenylketonuria is characterized by circulating osteoclast precursors and activated T cell increase;I Roato;PLoS One,2010
4. Increased spontaneous osteoclastogenesis from peripheral blood mononuclear cells in phenylketonuria;F Porta;J Inherit Metab Dis,2008
5. Cardiovascular defects among the progeny of mouse phenylketonuria females;JD McDonald;Pediatr Res,1997
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