Low Therapeutic Threshold for Hepatocyte Replacement in Murine Phenylketonuria-Reference-Cited by-同舟云学术

Low Therapeutic Threshold for Hepatocyte Replacement in Murine Phenylketonuria

Published:2005-08 Issue:2 Volume:12 Page:337-344
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Hamman Kelly,Clark Heather,Montini Eugenio,Al-Dhalimy Muhsen,Grompe Markus,Finegold Milton,Harding Cary O.

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference31 articles.

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3. Intellectual development in 12-year-old children treated for phenylketonuria;Azen;Am. J. Dis. Child.,1991

4. Gene therapy for phenylketonuria: phenotypic correction in a genetically deficient mouse model by adenovirus-mediated hepatic gene therapy;Fang;Gene Ther.,1994

5. Principles of hepatocyte repopulation;Laconi;Semin. Cell Dev. Biol.,2002

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